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Two fathers of children with rare diseases talk about starting biotech companies to try to create new therapies for their family members and others
Interviewed by MassBio CEO Kendalle Burlin O'Connell, Ilan Ganot describes co-founding Solid Biosciences in honor of his child with Duchenne muscular dystrophy and Daniel Fischer discusses co-founding Tevard Biosciences in honor of his child with Dravet syndrome. Chapters Intros - 1:11 Ilan Ganot | Starting a DMD company - 6:17 Daniel Fischer | Starting a Dravet company - 8:39 The Massachusetts ecosystem - 10:36 Being a CEO - 18:48 Advice for other parents - 23:43 Incentivizi
1 day ago
Solid Biosciences CEO Bo Cumbo discusses recent DMD data for the company's microdystrophin gene therapy, and explains the development and regulatory steps ahead
He describes data presented at the 2026 Muscular Dystrophy Association Annual Meeting, which showed biopsy and safety data for 20 patients who have been followed for 90 days and 3 who are out to a year. Plus, explaining the three FDA meetings that are key for the company.
Mar 25
The CEO of Solid Biosciences discusses today's data release of the company's microdystrophin gene therapy candidate for Duchenne muscular dystrophy
Bo Cumbo describes the efficacy biomarkers and safety profile they are seeing, and explains why he believes the cascade of observations...
Feb 18, 2025
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